Gene therapy is promising to be key in the battle against cancer, inherited disorders, and many other diseases. Decades worth of advances in this field have resulted in a growing number of successful clinical trials to develop safe and effective treatments. Over the past few years scientists have developed a number of new nucleic acid-based therapies, which continue to improve the versatility of these genetic-based treatment approaches. In this course, you will start by building a fundamental understanding of gene therapy, then dive deeper with an in-depth look at important trends, research and advances in gene therapy. You will gain a clear understanding of how gene therapy works, how it has developed and advanced, and how much potential it has.
This course is an elective course in the Stanford Genetics and Genomics Certificate.
You Will Learn
Basic principles for getting nucleic acids into cells and using viruses to transfer DNA
Proven and new approaches to clinical trials
How to effectively use genome editing tools
Methodologies for successful RNAi and expression of non-coding RNAs to regulate genes and treat disease
Adi Barzel, Lecturer, Stanford University
Maria Grazia, Roncarolo Professor of Pediatrics and of Medicine, Stanford University
Mark Kay, Professor of Genetics, Stanford University
*This certificate neither substitutes for, nor leads to, being board certified as a genetic counselor (ABGC) or clinical geneticist (ABMG)